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ePoster Presentations
Attendee Eposter Persons
K. Zhang
Editas Medicine
Poster Author Of 1 e-Poster
ePosters
Clinical genetics and therapeutics
299 - Correlations between Glucosylsphingosine (Lyso-GL-1) and Disease Severity and Response to Oral Eliglustat in Treatment-Naïve Adults with Gaucher Disease Type 1